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Paper published by Dr Francyne Kubaski:
Review
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Impact of enzyme replacement therapy and hematopoietic stem cell transplantation in patients with Morquio A syndrome
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Tomatsu S, Sawamoto K, Alméciga-Díaz CJ, Shimada T, Bober MB, Chinen Y, Yabe H, Montaño AM, Giugliani R, Kubaski F, Yasuda E, Rodríguez-López A, Espejo-Mojica AJ, Sánchez OF, Mason RW, Barrera LA, Mackenzie WG, Orii T
Drug Design, Development and Therapy 2015, 9:1937-1953
Published Date: 1 April 2015